PHAR40040 Emerging therapies: Cloning, gene therapy and stem cells

Academic Year 2024/2025

This module is core for stage 4 of the BSc degree in Pharmacology. This module investigates modern experimental strategies in the development of Gene-based (silencing, editing, replacement), Cell-Based (stem cell) and Drug-based therapeutic interventions. Specific examples of the application of these emerging approaches to treat inherited and age-related blindness will be critically discussed

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Curricular information is subject to change

Learning Outcomes:

On completion of this module students: 1. will appreciate the fundamentals of vision and vision loss, 2. comprehend the principles supporting development of gene-,cell- and drug-based therapeutic intervetnions for blindness and 3 demonstrate ability to critica;distinguish progress in development of these approcahes to treat inherited retinal degeneration and age-related macular degeneration.

Student Effort Hours: 
Student Effort Type Hours


Autonomous Student Learning




Approaches to Teaching and Learning:
The content is primarily of lectures that cover specific concepts and which direct the students to the primary literature for further study. Introductoy and review lectures are included at the start and mid-way. 
Requirements, Exclusions and Recommendations
Learning Recommendations:


Module Requisites and Incompatibles
PATH30060 - Genetics,perinatal,paediatric

Assessment Strategy  
Description Timing Open Book Exam Component Scale Must Pass Component % of Final Grade
Exam (In-person): Essay-based questions n/a Graded Yes


Carry forward of passed components
Resit In Terminal Exam
Autumn Yes - 2 Hour
Please see Student Jargon Buster for more information about remediation types and timing. 
Feedback Strategy/Strategies

• Feedback individually to students, post-assessment

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